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Research Articles

01.

PubMed.gov - January 21, 2021

Preclinical biodistribution, tropism, and efficacy of oligotrophic AAV/Olig001 in a mouse model of congenital white matter disease

03.

U.S. Department of Health & Human Services

A new version of GARD is in development

05.

ResearchGate.net - April 23, 2021

Canavan Disease as a Model for Gene Therapy-Mediated Myelin Repair

07.

Elsevier.com - Published 2016

N-acetylaspartate supports the energetic demands of developmental myelination via oligodendroglial aspartoacylase

02.

PubMed.gov - October 4, 2016

N-acetylaspartate supports the energetic demands of developmental myelination via oligodendroglial aspartoacylase

04.

Rowan University Research Center

Welcome to the Cell and Gene Therapy Center

06.

Science.org - December 19, 2012

Long-Term Follow-Up After Gene Therapy for Canavan Disease

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